News

The U.S. Food and Drug Administration is due to review data on deramiocel, a cell therapy up for approval for heart disease ...
A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.
For the second time, a person with DMD has died of acute liver failure after being treated with the one-time gene therapy Elevidys.
Caregiving means that columnist Betty Vertin sometimes misses out on activities with her children who don't have DMD. Finding balance is key.
Columnist Robin Stemple marks two anniversaries that forever altered his life. Despite the incredible challenges, he feels ...
As her only son without DMD plays in a statewide all-star football game, columnist Betty Vertin reflects on his tie to his brothers.
Marisa Wexler is a senior science writer for Muscular Dystrophy News with an MS in cellular and molecular pathology. She covers the latest news and information on a variety of muscular dystrophy ...
The U.S. Food and Drug Administration (FDA) granted platform technology designation to the viral vector used in SRP-9003, an investigational gene therapy for limb-girdle muscular dystrophy type 2E ...
Doctors can use several tests to diagnose muscular dystrophy (MD). A correct diagnosis gives patients an understanding of how their disease is likely to progress. It also helps doctors do a better job ...
Duchenne muscular dystrophy (DMD) is the most common form of muscular dystrophy, accounting for about a third of all muscular dystrophies. The condition, which leads to progressive deterioration of ...
Decker, who has limb-girdle muscular dystrophy (LGMD) type 2D, was honored at the Muscular Dystrophy Association (MDA)’s annual meeting, recently held in Dallas and virtually. “It’s always nice to be ...
Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...